We are a global, clinical-stage biotechnology company focused on the discovery, development and commercialization of innovative treatments for severe rare conditions with high unmet medical need.
We are committed to pursuing severe rare diseases with well-defined biology that can be targeted with therapies tailored to patients’ needs.
We are headquartered in Basel, Switzerland, with business operations in the New York area.
We are on a mission to build a leading, fully integrated global severe rare disease company using our patient-centric approach to identify and develop transformative medicines for the treatment of severe rare diseases.
Meet Our Team
We have a world-class team with deep expertise in severe rare diseases and a track record of success in research and development, commercialization and business development for innovative products targeting orphan conditions with high unmet medical needs.
We value and model the passion, energy and entrepreneurial mindset necessary to develop life-changing therapeutics.
Head of Global Clinical Development and Medical Affairs