About Us
We are a global, clinical-stage biotechnology company focused on the discovery, development and commercialization of innovative treatments for severe rare conditions with high unmet medical need.
We are committed to pursuing severe rare diseases with well-defined biology that can be targeted with therapies tailored to patients’ needs.
We are headquartered in Basel, Switzerland, with business operations in the New York area.

Our Mission
We are on a mission to build a leading, fully integrated global severe rare disease company using our patient-centric approach to identify and develop transformative medicines for the treatment of severe rare diseases.
Meet Our Team
We have a world-class team with deep expertise in severe rare diseases and a track record of success in research and development, commercialization and business development for innovative products targeting orphan conditions with high unmet medical needs.
We value and model the passion, energy and entrepreneurial mindset necessary to develop life-changing therapeutics.
Management Team

Luca Santarelli, M.D.
Founder and Chief Executive Officer and Board Member

Claudia D’Augusta, Ph.D.
Chief Financial Officer

Christian Meyer, M.D., Ph.D.
Chief Development Officer

Sarah Holland, Ph.D.
Chief Business Officer

Kevin Harris, MBA
Chief Commercial Officer

Alain Bernard, Ph.D.
Chief Technology Officer

Martine Mazzetti, MsPharm
Head of Project Leadership and Principal to the CEO

Nader N. Youssef M.D., MBA, FACG
Senior Vice President,
Head of Global Clinical Development and Medical Affairs
Head of Global Clinical Development and Medical Affairs
Board of Directors

Thomas F. Woiwode, Ph.D.
Board Member and Chair

Sandip Kapadia, MBA, CPA
Board Member

Chahra Louafi
Board Member

Luca Santarelli, M.D.
Founder and Chief Executive Officer and Board Member

Hans Schikan
Board Member

Stephen Squinto, Ph.D.
Board Member